Pipeline

Overview
Pipeline
Sigma-Tau Pharmaceuticals, Inc. is a research-based pharmaceutical company focused on the discovery of molecules and therapies to help improve the lives of people who suffer from rare diseases.

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Research Pipeline
Development Program Indication Development Stage
EZN-2279 (Polyethylene Glycol Recombinant Adenosine Deaminase [PEG-rADA]) For enzyme replacement therapy for adenosine deaminase (ADA) deficiency in patients with severe combined immunodeficiency disease (SCID) who are not suitable candidates for or who have failed bone marrow transplantation. Phase III
EZN-2285 (calaspargase pegol) Treatment of Acute Lymphoblastic Leukemia (ALL)  BLA/Preparation
Nuartez (artesunate) Injection in severe malaria Immediate treatment of severe and complicated falciparum malaria NDA/Preparation
STP-206 live biotherapeutic Prevention of necrotizing enterocolitis (NEC) Phase II
Xenbilox® (chenodeoxycholic acid) Capsules Treatment of cerebrotendinous xanthomatosis (CTX) NDA/Preparation